Project Details
Description
Regeneron siRNA SOD1 Trial
| Short title | ALN-SOD |
|---|---|
| Acronym | ALN-SOD-ALS-2351 |
| Status | Active |
| Effective start/end date | 5/07/25 → 16/10/29 |
First in Human Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Multiple Ascending Doses of Intrathecally Administered ALN-SOD in Participants with Amyotrophic Lateral Sclerosis and SOD1 Mutations
- Rowe, Dominic (Primary Chief Investigator)
- Delcourt, Candice (Associate Investigator)
- Kalband, Balaji (Associate Investigator)
- Gan, Richard (Research Coordinator)
- Bayeh, Paula (Research Coordinator)
Project: Research