Combined enzyme replacement and haematopoietic stem cell transplantation in Hurler syndrome

Sunita Bijarnia, Peter Shaw, Anne Vimpani, Robert Smith, Verity Pacey, Helen O'Grady, John Christodoulou, David Sillence*

*Corresponding author for this work

Research output: Contribution to journalArticle

9 Citations (Scopus)

Abstract

We report the long-term follow-up of successful treatment of mucopolysaccharidosis type I H (MPS IH, Hurler syndrome) with combined enzyme replacement therapy and haematopoietic progenitor stem cell transplant.

Original languageEnglish
Pages (from-to)469-472
Number of pages4
JournalJournal of Paediatrics and Child Health
Volume45
Issue number7-8
DOIs
Publication statusPublished - Jul 2009
Externally publishedYes

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